Case Reports:
Small bowel GIST harboring concurrent KIT exon 9 duplication and SDHC mutation: A case report
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Cameron B. Speyer1, Kyle D. Klingbeil1,2, Manando Nakasaki3, Sarah M. Dry3, Arun S. Singh4, Karo K. Arzoo4, Fritz C. Eilber1,2 and Joseph G. Crompton1,2
1 Department of Surgery, Division of Surgical Oncology, UCLA David Geffen School of Medicine, Los Angeles, CA 90095, USA
2 Jonsson Comprehensive Cancer Center, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, CA 90095, USA
3 Department of Pathology, University of California Los Angeles, Los Angeles, CA 90095, USA
4 Department of Medicine, Division of Hematology-Oncology, University of California Los Angeles, Los Angeles, CA 90095, USA
Correspondence to:
| Joseph G. Crompton, | email: | [email protected] |
Keywords: GIST; KIT duplication; SDHC mutation; genetic testing; case report
Received: January 05, 2026 Accepted: March 17, 2026 Published: May 04, 2026
ABSTRACT
Gastrointestinal stromal tumors (GISTs) are molecularly defined by oncogenic alterations that predict clinical behavior and response to therapy. Activating mutations in KIT or PDGFRA characterize most GISTs and confer sensitivity to imatinib, whereas succinate dehydrogenase (SDH)–deficient GISTs lack these mutations and are typically imatinib resistant. These molecular subtypes are generally considered mutually exclusive. We report a rare case of a small bowel GIST harboring both a somatic KIT exon 9 A502_Y503 duplication and a germline inactivating SDHC mutation (p.R50C). The patient received neoadjuvant high-dose imatinib with a marked radiographic and metabolic response, followed by complete surgical resection. Pathology demonstrated spindle cell GIST with significant treatment effect and retained SDHB expression. This case suggests that oncogenic KIT signaling may remain the dominant driver of GIST behavior despite the presence of a germline SDHC mutation and highlights the importance of integrated molecular interpretation in GIST management.